Item 8.01 Other Events.
On January 8, 2021, Ultragenyx Pharmaceutical Inc. (the "Company") issued a
press release announcing positive longer-term safety and efficacy data from the
first three cohorts of the Company's ongoing Phase 1/2 studies of DTX401 an
investigational adeno-associated virus ("AAV") gene therapy for the treatment of
Glycogen Storage Disease Type Ia (GSDIa), and DTX301, an AAV gene therapy for
the treatment of ornithine transcarbamylase (OTC) deficiency, and other updates
related to the Company's gene therapy portfolio.
A copy of the Press Release is filed as Exhibit 99.1 and incorporated herein by
reference.
Item 9.01 Financial Statements and Exhibits.
Exhibit No. Description
99.1 Press Release, dated January 8, 2021.
104 The cover page from the Company's Current Report on Form 8-K dated
January 8, 2021 formatted in Inline XBRL.
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